Ultragenyx Pharmaceutical Inc.

Ultragenyx Pharmaceutical Inc.

RARE
Ultragenyx Pharmaceutical Inc.US flagNASDAQ Global Select
15.30
USD
+0.45
- -
1.51BMarket Cap
2013 Y
2014 Y
2015 Y
2016 Y
2017 Y
2018 Y
2019 Y
2020 Y
2021 Y
2022 Y
2023 Y
2024 Y
2025 Y
TTM
Revenue per Share
- -
- -
- -
- -
0.06
1.03
1.83
4.45
5.18
5.2
5.9
6.19
6.83
7.13
Basic EPS, GAAP
-1.73
-2.25
-3.96
-6.21
-7.12
-3.97
-7.12
-3.07
-6.7
-10.12
-8.25
-6.28
-5.83
-5.83
Free Cash Flow per Basic Share
-1.09
-1.63
-3.02
-4.32
-6.05
-5.92
-6.54
-2.89
-6.07
-7.53
-7.1
-4.79
-4.94
-4.91
Dividend per Share
- -
0.15
- -
- -
- -
- -
- -
- -
- -
- -
- -
- -
- -
- -
Book Value per Share
-2.57
5.79
13.66
11.49
8.68
11.97
11.3
17.28
13.3
5.02
3.35
2.76
-0.83
-2.95
Tangible Book Value per Share
-2.57
5.79
13.66
11.49
4.47
8.56
8.31
14.65
10.78
2.11
0.79
0.36
-3.11
-5.14
Basic Weighted Avg Shares
29
29
37
40
42
50
57
61
68
70
74
91
99
101
Sales/Revenue/Turnover
- -
- -
- -
- -
3
51
104
271
351
363
434
560
673
717
Operating Margin (%)
- -
- -
- -
-186,471.43
-12,593.49
-721.18
-408.98
-121.8
-108.63
-178.6
-131.11
-95.71
-79.49
-73.64
Depreciation Expense
- -
1
1
3
6
20
9
12
13
18
26
36
35
33
Net Income, GAAP
-35
-60
-146
-246
-302
-198
-403
-187
-454
-707
-607
-569
-575
-586
Effective Tax Rate (%)
- -
- -
- -
- -
- -
- -
- -
- -
- -
- -
- -
- -
- -
- -
Profit Margin (%)
- -
- -
- -
-184,867.67
-11,567.34
-383.75
-388.31
-68.84
-129.2
-194.71
-139.86
-101.61
-85.44
-81.7
Working Capital
49
181
422
341
199
448
748
1,106
675
623
452
473
567
255
LT Debt
- -
- -
- -
- -
- -
- -
30
39
31
20
31
30
24
- -
Total Equity
50
185
531
474
383
609
654
1,154
923
352
275
262
-73
-284
Return on Invested Capital (%)
- -
- -
- -
- -
- -
- -
- -
- -
- -
- -
- -
- -
- -
- -
Return on Capital (%)
- -
- -
- -
- -
- -
- -
- -
- -
- -
- -
- -
- -
- -
- -
Return on Common Equity (%)
- -
- -
-40.67
-48.93
-70.48
-39.83
-63.79
-20.64
-43.72
-110.96
-193.34
-214.55
- -
-325.74

Capital Structure

FRC

in mil. unless spec.
Dec'25
Mar'26
Jun'26
ST Debt
12
- -
- -
LT Borrowings
- -
- -
- -
LT Finance Leases
24
- -
- -
Preferred Equity and Hybrid Capital
- -
- -
- -
Shares Outstanding
96
98
99
Market Capitalization
2,219
2,060
3,292

Working Capital

FRC

in mil. unless spec.
Dec'25
Mar'26
Jun'26
Total Current Assets
951
657
606
Cash, Cash Equivalents & STI
680
413
292
Accounts Receivable, Net
158
121
200
Inventories
52
55
59
Total Current Liabilities
384
325
351
Payables & Accruals
239
175
188
ST Debt
12
- -
- -
Deferred Revenue
- -
- -
- -

Growth Rates

FRC

in mil. unless spec.

(avg. rate of change)

10 years
5 years
1 year
Total Equity
-12.36%
-47.29%
-127.86%
Free Cash Flow
24.84%
31.23%
12.21%
Net Income, GAAP
28.7%
35.95%
1.05%
Sales/Revenue/Turnover
- -
20.34%
20.18%
Total Cash Common Dividend
- -
- -
- -

Quarterly Revenue

FRC

in mil. unless spec.

Year

Q1
Q2
Q3
Q4
FY
2024
109
147
139
165
560
2025
139
167
160
207
673
2026
136
214
- -
- -
- -

Quarterly Earnings Per Share

FRC

in mil. unless spec.

Year

Q1
Q2
Q3
Q4
FY
2024
-2.03
-1.52
-1.4
-1.39
-6.28
2025
-1.57
-1.17
-1.81
-1.29
-5.83
2026
-1.84
-0.9
- -
- -
- -

Quarterly Dividends Per Share

FRC

in mil. unless spec.

Year

Q1
Q2
Q3
Q4
FY
2024
- -
- -
- -
- -
- -
2025
- -
- -
- -
- -
- -
2026
- -
- -
- -
- -
- -

Company Description

CEO
Emil D. Kakkis
Full Time Employees
1,371
Sector
Healthcare
Industry
Biotechnology
Address
60 Leveroni Court Novato CA United States of America 94949
IPO Date
Jan 31, 2014
Business
Ultragenyx Pharmaceutical Inc. (Nasdaq: RARE) is a biopharmaceutical company focused on the development and commercialization of innovative therapies for rare and ultrarare genetic diseases. Founded in 2010 and headquartered in Novato, California, the company offers approved products including Crysvita (burosumab) for X-linked hypophosphatemia and tumor-induced osteomalacia; Mepsevii for mucopolysaccharidosis VII; and Dojolvi (triheptanoin) for long-chain fatty acid oxidation disorders; alongside a robust pipeline targeting conditions such as Angelman syndrome with GTX-102. Ultragenyx operates globally, with commercial presence in North America, Europe, and select international markets, serving patients through specialized support programs like UltraCare. In recent developments, Ultragenyx sold a portion of future North American royalties on Crysvita to OMERS Life Sciences for $400 million in November 2025; reported third quarter 2025 financial results with total revenue guidance of $640 million to $670 million; dosed the first patient in the Aurora study for GTX-102 in Angelman syndrome in October 2025; and appointed Eric Olson as Chief Business Officer in September 2025.

Company News

  • Why Is Ultragenyx (RARE) Up 6.4% Since Last Earnings Report?

  • RARE Stock Down 46% as Phase III Angelman Syndrome Study Misses Goals

  • QUICK SPARK: Pharma Bro Martin Shkreli Says Ultragenyx Should Be M&A Target

  • Ultragenyx Forced To Cut Costs After Disappointing Phase 3 Results

  • Here Are Thursday’s Top Wall Street Analyst Research Calls: Broadcom, Deere & Company, Dell Technologies, Devon Energy, Moderna, Permian Resources, PG&E, Thermo Fisher, Viper Energy, and More

  • Ultragenyx Stock Sinks 47% on Drug Trial Failure. Why Wall Street Isn't Giving Up Yet.

  • Ultragenyx shares crater after Angelman syndrome drug fails late-stage trial

  • Ultragenyx's rare disease drug fails in late-stage trial; shares plunge

  • Ultragenyx Announces Phase 3 Aspire results in Angelman Syndrome

  • Ultragenyx Announces the Publication of a Successful 96-Week Randomized, Placebo-Controlled Trial with Crossover Treatment of GENGLYCOS™ (also known as DTX401) AAV Gene Therapy in GSDIa in The Journal of Inherited Metabolic Disease

  • 4 Rare Disease Drugmakers With Strong Long-Term Growth Prospects

  • Ultragenyx Reports Inducement Grant Under Nasdaq Listing Rule 5635(c)(4)

  • 164,813 Shares in Ultragenyx Pharmaceutical Inc. $RARE Bought by Deutsche Bank AG

  • RARE Stock Gains on FDA Nod for Rare Disease Gene Therapy Genglycos

  • Ultragenyx Nabs FDA Nod for First Gene Therapy

  • Ultragenyx Wins FDA Approval for GENGLYCOS, Its First Gene Therapy

  • Ultragenyx Pharmaceutical Inc. (RARE) Discusses FDA Approval of Gene Therapy for Glycogen Storage Disease Type 1a Transcript

  • Ultragenyx's gene therapy for rare metabolic disorder secures US FDA nod

  • Ultragenyx Announces U.S. FDA Approval of GENGLYCOS™ Gene Therapy, the First-Ever FDA-Approved Treatment Designed to Treat the Underlying Cause of Glycogen Storage Disease Type Ia (GSDIa)

  • Ultragenyx: Undervalued Ahead Of Two FDA Decisions